P.353FIREFISH Part 1: 16-month safety and exploratory outcomes of risdiplam (RG7916) treatment in infants with type 1 spinal muscular atrophy
Giovanni Baranello,
Laurent Servais,
John Day,
Nicolas Deconinck,
Eugenio Mercuri,
Andrea Klein,
Basil T. Darras,
Riccardo Masson,
Heidemarie Kletzl,
Yumi Cleary,
Neuromuscular Disorders · 2019 · 17 citations · 0 references