Publication | Closed Access

Safety and efficacy of deferiprone for pantothenate kinase-associated neurodegeneration: a randomised, double-blind, controlled trial and an open-label extension study

Neurodegenerative DiseasesPantothenate Kinase-associated NeurodegenerationOpen-label Extension StudyMedicineNeuropharmacologyNeurochemical BiomarkersPharmacotherapyNeurologyNeuroscienceNeuroprotectionPharmacologyNovel Therapy