Journal of Exercise Rehabilitation · 2019 · 12 citations · 13 references
MedicinePediatricsRehabilitation MedicineExercise PhysiologyNeuromuscular DisordersPediatric Rehabilitation MedicineExercise TrainingNeuromuscular Disorder RehabilitationNeuromuscular Function AssessmentNeuromuscular RehabilitationPhysical Activity For ChildrenSpinal Muscular AtrophyAerobic Training AdaptationAerobic Training In ChildrenGross Motor Function AssessmentPediatric Neuromuscular Disease TreatmentPediatric Neuromuscular DisordersPediatric Spinal Muscular AtrophyQuality Of Life EndpointsSpinal Muscular Atrophy Rehabilitation
This study examined the effect of two different aerobic training modalities in a boy with spinal muscular atrophy type II. Motor functions were measured with Hammersmith Functional Motor Scale (HFMS) and Gross Motor Function Measure (GMFM). Spirometry was utilized for assessing pulmonary functions and PedsQL 3.0 Neuromuscular module was utilized for quality of life of child. Ergometer training was applied 3 times per week for the duration of 12 weeks. After 6 weeks of wash-out period, aquatherapy was applied for twice a week for the duration of 12 weeks. HFMS and GMFM scores, and pulmonary functions of the child and quality of life scores of his parents were improved during both modalities. These improvements were largely maintained during 1-year follow-up. This study showed that both modalities had similar effects on our case's pulmonary, motor functions and quality life of himself and parents. It will be a guide for researchers working in the area of children with neuromuscular disorders regarding plan and diversification of therapy program.
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Martin R. Miller, J. Hankinson, Vito Brusasco et al. · European Respiratory Journal · 2005 · 15.7K citations · Full text
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy
Richard S. Finkel, Eugenio Mercuri, Basil T. Darras et al. · New England Journal of Medicine · 2017 · 2.3K citations · Full text
Consensus Statement for Standard of Care in Spinal Muscular Atrophy
Ching H. Wang, Richard S. Finkel, Enrico Bertini et al. · Journal of Child Neurology · 2007 · 946 citations
Marion Main, Harvey Kairon, Eugenio Mercuri et al. · European Journal of Paediatric Neurology · 2003 · 241 citations
Medicine, Neurology, Pediatrics +17