Safety, tolerability and pharmacokinetics of oral venglustat in Parkinson disease patients with a GBA mutation

Michel Peterschmitt, Thomas Gasser, Stuart Isaacson, Jaime Kulisevsky, Pablo Mir, Tanya Simuni, Anne‐Marie Wills, Leonor Correia Guedes, Per Svenningsson, Cheryl Waters,

Molecular Genetics and Metabolism · 2019 · 18 citations · 0 references

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