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Publication | Open Access

Intrathecal heparan-N-sulfatase in patients with Sanfilippo syndrome type A: A phase IIb randomized trial

DOIFull Paper Access

45

Citations

9

References

2018

Year

Frits A. Wijburg, Chester B. Whitley, Joseph Muenzer, Serena Gasperini, Mireia del Toro, Nicole Muschol, Maureen Cleary, Caroline Sevin, Elsa Shapiro, Parul Bhargava,
Molecular Genetics and Metabolism

Abstract

ClinicalTrials.govNCT02060526; EudraCT 2013-003450-24.

References

YearCitations

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