Publication | Open Access

Safety and efficacy of olesoxime in patients with type 2 or non-ambulatory type 3 spinal muscular atrophy: a randomised, double-blind, placebo-controlled phase 2 trial

Placebo-controlled Phase 2Chronic Musculoskeletal ConditionType 2Clinical TrialsSpinal Muscular AtrophyMedicineSpinal DisorderOrthopaedic SurgeryNeuromusculoskeletal Disorder