Optimising gene repair strategies in cell culture

Multi-Organ, Multi-Lineage Engraftment by a Single Bone Marrow-Derived Stem Cell

Diane S. Krause, Neil D. Theise, Michael I. Collector et al. · Cell · 2001 · 2.7K citations · Full text

Life Sciences, Cell Biology, Regenerative Medicine +13

Gene Therapy of Human Severe Combined Immunodeficiency (SCID)-X1 Disease

Marina Cavazzana, Salima Hacein‐Bey, Geneviève de Saint Basile et al. · Science · 2000 · 2.6K citations

Life Sciences, Genetics, Immunology +17

Evidence for Stem-Cell Niches in the Tracheal Epithelium

Duncan W. Borthwick, Mariam Shahbazian, Q. Todd Krantz et al. · American Journal of Respiratory Cell and Molecular Biology · 2001 · 414 citations

Life Sciences, Biology, Cell Biology +14

Targeted gene correction of episomal DNA in mammalian cells mediated by a chimeric RNA.DNA oligonucleotide.

Kyung Chul Yoon, Allyson Cole-Strauss, Eric B. Kmiec · Proceedings of the National Academy of Sciences · 1996 · 220 citations · Full text

Life Sciences, Biotechnology, Molecular Biology +13

Targeted gene correction by small single-stranded oligonucleotides in mammalian cells

Olga Igoucheva, Vitali Alexeev, Kyung Chul Yoon · Gene Therapy · 2001 · 152 citations

Life Sciences, Genetics, Molecular Biology +16