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Deletion of exons 3−9 encompassing a mutational hot spot in the DMD gene presents an asymptomatic phenotype, indicating a target region for multiexon skipping therapy

Transcriptional RegulationSystems BiologyEngineeringGenetic DisorderMedicineGeneticsExons 3−9Dmd Gene PresentsMolecular GeneticsDisease Gene IdentificationMultiexon Skipping TherapyGene ExpressionMolecular DiagnosticsGene Deletion Data