Familial lecithin:cholesterol acyltransferase deficiency: First-in-human treatment with enzyme replacement

Robert D. Shamburek, Rebecca Bakker‐Arkema, Bruce J. Auerbach, Brian R. Krause, Reynold Homan, Marcelo Amar, Lita A. Freeman, Alan T. Remaley

Journal of clinical lipidology · 2015 · 94 citations · 17 references

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