Publication | Open Access
Enzyme replacement therapy with galsulfase in 34 children younger than five years of age with MPS VI
Dafne Dain Gandelman Horovitz,
Tatiana Sá Pacheco Carneiro Magalhães,
Angelina Xavier Acosta,
Erlane Marques Ribeiro,
Liane R. Giuliani,
Durval Batista Palhares,
Chong Ae Kim,
Ana Paula,
Marcelo Kerstenestzy,
Mara Albonei Dudeque Pianovski,
Molecular Genetics and Metabolism