Publication | Closed Access
Oral 9-cis retinoid for childhood blindness due to Leber congenital amaurosis caused by RPE65 or LRAT mutations: an open-label phase 1b trial
99
Citations
25
References
2014
Year
Ocular DiseaseRetinaOphthalmologyOral 9-CisGeneticsChildhood BlindnessGlaucomaOcular PathologyRetinal TherapiesLeber Congenital AmaurosisMedicine
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