Publication | Open Access
Functional correction by antisense therapy of a splicing mutation in the GALT gene
17
Citations
27
References
2014
Year
Functional CorrectionGene TherapiesNatural SciencesGeneticsRna SplicingGenetic EngineeringMolecular BiologyMolecular GeneticsGene EditingAntisense TherapyGalt GeneGene ExpressionMedicineSplicing VariantGenome Editing
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