Publication | Open Access
Gene silencing of EXTL2 and EXTL3 as a substrate deprivation therapy for heparan sulphate storing mucopolysaccharidoses
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Citations
35
References
2009
Year
EngineeringMedicineBiotechnologyGenetic EngineeringMolecular BiologyBiochemical GeneticsMolecular GeneticsGene SilencingSubstrate Deprivation TherapyLysosomal Storage DiseaseBiomolecular Engineering
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