Gene Therapy · 2007 · 118 citations · 50 references
MedicineGeneticsOphthalmologyGene TherapyOcular DiseaseOcular GeneticsOcular Gene DeliveryOcular Gene TherapyRetinal DegenerationRetinal DiseaseRetinal DisordersRetinal Pigment EpitheliumInherited Retinal Disease Gene TherapyLentiviral Gene TransferLentiviral TransgenesisRetinal Disease MechanismsRetinal Disease ModelsRetinal Regeneration Gene TherapyUsher Syndrome
50
A Third-Generation Lentivirus Vector with a Conditional Packaging System
Tom Dull, Romain Zufferey, Michael T. Kelly et al. · Journal of Virology · 1998 · 3.4K citations · Full text
Jane C. Burns, T Friedmann, Wolfgang Driever et al. · Proceedings of the National Academy of Sciences · 1993 · 1.4K citations
Gene therapy restores vision in a canine model of childhood blindness
Gregory M. Acland, Jharna Ray, Qí Zhāng et al. · Nature Genetics · 2001 · 1.2K citations
Defective myosin VIIA gene responsible for Usher syndrome type IB
Dominique Well, Stéphane Blanchard, Josseline Kaplan et al. · Nature · 1995 · 1.1K citations