Short-Term Enzyme Replacement in the Murine Model of Sanfilippo Syndrome Type B

References

Page 1

	Year	Citations
Replacement Therapy for Inherited Enzyme Deficiency — Macrophage-Targeted Glucocerebrosidase for Gaucher's Disease Norman W. Barton, Roscoe O. Brady, James M. Dambrosia, New England Journal of Medicine	1991	1.3K
Enzyme Therapy in Type 1 Gaucher Disease: Comparative Efficacy of Mannose-Terminated Glucocerebrosidase from Natural and Recombinant Sources Gregory A. Grabowski Annals of Internal Medicine	1995	444
Infusion of α-galactosidase A reduces tissue globotriaosylceramide storage in patients with Fabry disease Raphael Schiffmann, Gary J. Murray, DA Treco, Proceedings of the National Academy of Sciences GlycobiologyPathologyTissue Globotriaosylceramide StorageTranslational MedicineFabry Disease	2000	345
An electron microscope autoradiographic study of the carbohydrate recognition systems in rat liver. I. Distribution of 125I-ligands among the liver cell types. A L Hubbard, Glynn Wilson, Gilbert Ashwell, The Journal of Cell Biology Endothelial CellsGlycobiologyPolysaccharideBioanalysisHepatotoxicity	1979	311
Murine mucopolysaccharidosis type VII. Characterization of a mouse with beta-glucuronidase deficiency. E H Birkenmeier, Muriel T. Davisson, Wesley G. Beamer, Journal of Clinical Investigation Mps ViiImmunodeficienciesGeneticsImmunologyPathology	1989	290
Noninvasive gene targeting to the brain Ningya Shi, William M. Pardridge Proceedings of the National Academy of Sciences	2000	254
Mouse model of Sanfilippo syndrome type B produced by targeted disruption of the gene encoding α-<i>N</i>-acetylglucosaminidase Hong Hua Li, Wei-Hong Yu, Nora Rozengurt, Proceedings of the National Academy of Sciences	1999	211
Enzyme replacement therapy for murine mucopolysaccharidosis type VII. Mark S. Sands, Carole Vogler, John W. Kyle, Journal of Clinical Investigation Multiple InjectionsMps ViiMps Vii MiceLaboratory ImmunologyEnzyme Replacement Therapy	1994	200
A mouse model for mucopolysaccharidosis type III A (Sanfilippo syndrome) Mantu Bhaumik, Vivienne Muller, Tina Rozaklis, Glycobiology	1999	187
Correction of lysosomal storage in the liver and spleen of MPS VII mice by implantation of genetically modified skin fibroblasts Philippe Moullier, Delphine Bohl, Jean‐Michel Heard, Nature Genetics Regenerative MedicineKnockout MouseMps Vii MiceXenotransplantationCutaneous Biology	1993	178

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