Concepedia

Publication | Open Access

Adeno‐associated virus gene repair corrects a mouse model of hereditary tyrosinemia in vivo†‡

DOIFull Paper Access

136

Citations

35

References

2009

Year

Nicole K. Paulk, Karsten Wursthorn, Zhongya Wang, Milton J. Finegold, Mark A. Kay, Markus Grompe
Hepatology

Abstract

AAV-mediated gene repair is feasible in vivo and can functionally correct an appropriate selection-based metabolic liver disease in both adults and neonates.

References

YearCitations

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