Concepedia

Preclinical correction of human Fanconi anemia complementation group A bone marrow cells using a safety-modified lentiviral vector

Pamela S. Becker, Jason Taylor, Grant D. Trobridge, Xin Zhao, Brian C. Beard, Sylvia Chien, Jennifer E. Adair, Donald B. Kohn, John E. Wagner, Akiko Shimamura,

Gene Therapy · 2010 · 40 citations · 23 references

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References

23

Self-Inactivating Lentivirus Vector for Safe and Efficient In Vivo Gene Delivery

Romain Zufferey, Thomas J. Dull, Ronald J. Mandel et al. · Journal of Virology · 1998 · 1.8K citations · Full text

Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element Enhances Expression of Transgenes Delivered by Retroviral Vectors

Romain Zufferey, John E. Donello, Didier Trono et al. · Journal of Virology · 1999 · 1K citations · Full text

Gene transfer by lentiviral vectors is limited by nuclear translocation and rescued by HIV-1 pol sequences

Antonia Follenzi, Laurie Ailles, Silvia Bakovic et al. · Nature Genetics · 2000 · 933 citations

, , +14

Hematologic abnormalities in Fanconi anemia: an International Fanconi Anemia Registry study [see comments]

A Butturini, Gale Rp, PC Verlander et al. · Blood · 1994 · 384 citations · Full text

Reverse mosaicism in Fanconi anemia: natural gene therapy via molecular self-correction

M Gross, Helmut Hanenberg, Stephan Lobitz et al. · Cytogenetic and Genome Research · 2002 · 251 citations

, , +16