Enzyme replacement therapy for mucopolysaccharidosis VI: A phase 3, randomized, double-blind, placebo-controlled, multinational study of recombinant human N-acetylgalactosamine 4-sulfatase (recombinant human arylsulfatase B or rhASB) and follow-on, open-label extension study

Publication | Closed Access

DOI

361

Citations

References

2006

Year

Paul Harmatz, Roberto Giugliani, Ida Vanessa Döederlein Schwartz, Nathalie Guffon, Elisa Leão Teles, Clara Sá-Miranda, J. E. Wraith, Michael Beck, Laila Arash, Maurizio Scarpa,

The Journal of Pediatrics

Translational MedicinePhase 3Enzyme Replacement TherapyImmunologyPathologyTranslational ResearchMultinational StudyMedicineLysosomal Storage DiseaseDrug Discovery