Nature Genetics · 1993 · 342 citations · 31 references
Life SciencesMolecular BiologyMolecular PharmaceuticsGene ExpressionGene TherapyMolecular VirologyPlasma ProteinsViral Gene ExpressionAdeno-associated Viral VectorsAdenoviral VectorsAdenovirus BiologyAdenovirus VectorsFactor Ix Physiology
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The Metabolic Basis of Inherited Diseases
R.K. Winkelmann · Archives of Dermatology · 1972 · 1.8K citations