Agalsidase beta treatment is associated with improved quality of life in patients with Fabry disease: Findings from the Fabry Registry

Torquil Watt, Alessandro P. Burlina, Chiara Cazzorla, Dorothee Schönfeld, Maryam Banikazemi, Robert J. Hopkin, Ana María Martins, Katherine B. Sims, Dana Beitner‐Johnson, Fanny O’Brien,

Genetics in Medicine · 2010 · 83 citations · 32 references

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