Concepedia

Publication | Closed Access

Enzyme replacement therapy with agalsidase alfa in children with Fabry disease

DOI

110

Citations

18

References

2006

Year

Uma Ramaswami, S. Wendt, Guillem Pintos‐Morell, Rossella Parini, Catharina Whybra, Jose A. Leal, Francesca Santus, Michael Beck
Acta Paediatrica

Abstract

ERT with agalsidase alfa in children with Fabry disease is well tolerated and, in the short term, appears to decrease pain and to improve pain-related QoL.

References

YearCitations

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