Concepedia

AAV1 Mediated Co-expression of Formylglycine-Generating Enzyme and Arylsulfatase A Efficiently Corrects Sulfatide Storage in a Mouse Model of Metachromatic Leukodystrophy

Toshiyuki Kurai, Sanae Hisayasu, Ryo Kitagawa, Makoto Migita, Hidenori Suzuki, Yukihiko Hirai, Takashi Shimada

Molecular Therapy · 2006 · 45 citations · 27 references

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References

27

A SIMPLE METHOD FOR THE ISOLATION AND PURIFICATION OF TOTAL LIPIDES FROM ANIMAL TISSUES

Jordi Folch, Marjorie B. Lees, G H S Stanley · Journal of Biological Chemistry · 1957 · 64.9K citations · Full text

, , +11

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

Guangping Gao, Mauricio R. Alvira, Lili Wang et al. · Proceedings of the National Academy of Sciences · 2002 · 1.5K citations · Full text

, , +15

Differential staining of acid glycosaminoglycans (mucopolysaccharides) by Alcian blue in salt solutions

J. E. Scott, J. Dorling · Histochemistry and Cell Biology · 1965 · 1.1K citations

, , +13

Expression vector system based on the chicken β-actin promoter directs efficient production of interleukin-5

Jun‐ichi Miyazaki, Kimi Araki, Fumi Tashiro et al. · Gene · 1989 · 457 citations

, , +11

A recombinant plasmid from which an infectious adeno-associated virus genome can be excised in vitro and its use to study viral replication

R. Jude Samulski, Long‐Sheng Chang, Thomas Shenk · Journal of Virology · 1987 · 444 citations · Full text

, , +17