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Long‐term effectiveness of enzyme replacement therapy in Fabry disease: results from the NCS‐LSD cohort study

DOI

52

Citations

35

References

2014

Year

Lindsey Anderson, Katrina Wyatt, William Henley, Vasilis Nikolaou, S. Waldek, Derralynn Hughes, Gregory M. Pastores, Stuart Logan
Journal of Inherited Metabolic Disease

Abstract

These data provide some further evidence on the long-term effectiveness of ERT in adults with Fabry disease, but evidence of effectiveness could not be demonstrated in children.

References

YearCitations

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