Iron‐related MRI images in patients with pantothenate kinase–associated neurodegeneration (PKAN) treated with deferiprone: Results of a phase II pilot trial

Giovanna Zorzi, Federica Zibordi, Luisa Chiapparini, Enrico Bertini, Lidia Russo, Antonio Piga, Filomena Longo, Barbara Garavaglia, Domenico Aquino, M. Savoiardo,

Movement Disorders · 2011 · 140 citations · 20 references

Abstract

Future trials assessing the clinical efficacy of chelating therapy should consider early symptomatic patients and a longer treatment period.

References

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