Publication | Closed Access
Early-Onset Severe Neurological Involvement and D409H Homozygosity in Gaucher Disease: Outcome of Enzyme Replacement Therapy
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Citations
15
References
2002
Year
Neurodegenerative DiseasesAlzheimer's DiseaseGaucher DiseaseMendelian DisorderEnzyme Replacement TherapyNeurological DisorderGeneticsGenetic DisorderPathologyDegenerative DiseaseSubstrate Reduction TherapyNeurologyD409h HomozygosityNeurodegenerationNeuropathologyMedicine
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