AGADA Biosciences

Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping

Paula R. Clemens, Vamshi K. Rao, Anne M. Connolly et al. · JAMA Neurology · 2020 · 250 citations · Full text

Genetic tool development in marine protists: emerging model organisms for experimental cell biology

Drahomíra Faktorová, R. Ellen R. Nisbet, José A. Fernández Robledo et al. · Nature Methods · 2020 · 162 citations · Full text

Vamorolone targets dual nuclear receptors to treat inflammation and dystrophic cardiomyopathy

Christopher R. Heier, Qing Yu, Alyson A. Fiorillo et al. · Life Science Alliance · 2019 · 77 citations · Full text

Heart Failure, Immunology, Cardiovascular Pharmacology +17

Ryanodine channel complex stabilizer compound S48168/ARM210 as a disease modifier in dystrophin‐deficient <i>mdx</i> mice: proof‐of‐concept study and independent validation of efficacy

Roberta Francesca Capogrosso, Paola Mantuano, Kitipong Uaesoontrachoon et al. · The FASEB Journal · 2017 · 57 citations · Full text

Foxf2 plays a dual role during transforming growth factor beta-induced epithelial to mesenchymal transition by promoting apoptosis yet enabling cell junction dissolution and migration

Nathalie Meyer‐Schaller, Chantal Heck, Stefanie Tiede et al. · Breast Cancer Research · 2018 · 46 citations · Full text