Statistics
Publications
19
Citations
1.5K
H-Index
18
Active since
2002
Ksenija Gorni is an author at Children's National specializing in muscular dystrophy, medicine, and duchenne muscular dystrophy pharmacotherapy.
Publications per year
2002–2022
19
19
Prevalence of congenital muscular dystrophy in Italy
Alessandra Graziano, Flaviana Bianco, Adele D’Amico et al. · Neurology · 2015 · 104 citations · Full text
Medicine, Genetics, Pediatrics +14
Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy
Jean K. Mah, Paula R. Clemens, Michela Guglieri et al. · JAMA Network Open · 2022 · 88 citations · Full text
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