Sami Khella

Eplontersen for Hereditary Transthyretin Amyloidosis With Polyneuropathy

Teresa Coelho, Wilson Marques, Noel R. Dasgupta et al. · JAMA · 2023 · 171 citations · Full text

Precision targeting of autoantigen-specific B cells in muscle-specific tyrosine kinase myasthenia gravis with chimeric autoantibody receptor T cells

Sangwook Oh, Xuming Mao, Sílvio M. Vieira et al. · Nature Biotechnology · 2023 · 149 citations · Full text

Quality of life in idiopathic intracranial hypertension at diagnosis

Kathleen B. Digre, Bonnie Bruce, Michael McDermott et al. · Neurology · 2015 · 102 citations · Full text

Design and Rationale of the Global Phase 3 NEURO-TTRansform Study of Antisense Oligonucleotide AKCEA-TTR-LRx (ION-682884-CS3) in Hereditary Transthyretin-Mediated Amyloid Polyneuropathy

Teresa Coelho, Yukio Ando, Merrill D. Benson et al. · Neurology and Therapy · 2021 · 54 citations · Full text

Prospective study of proton beam radiation therapy for adjuvant and definitive treatment of thymoma and thymic carcinoma: Early response and toxicity assessment

Jennifer Vogel, Abigail T. Berman, Liyong Lin et al. · Radiotherapy and Oncology · 2016 · 52 citations

Early Response, Radiation Therapy, Medicine +10