Soon-Chai Low

Efficacy and safety of vutrisiran for patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: a randomized clinical trial

David Adams, Ivailo Tournev, Mark Taylor et al. · Amyloid · 2022 · 379 citations · Full text

Medicine, Neurology, Pharmacotherapy +13

Probiotics for Constipation in Parkinson Disease

Ai Huey Tan, Shen‐Yang Lim, Kah Kian Chong et al. · Neurology · 2020 · 209 citations

Life Sciences, Neuroscience, Pharmacotherapy +12

Long-term safety and efficacy of patisiran for hereditary transthyretin-mediated amyloidosis with polyneuropathy: 12-month results of an open-label extension study

David Adams, Michael Polydefkis, Alejandra González‐Duarte et al. · The Lancet Neurology · 2020 · 156 citations

Medicine, Neurology, Pharmacotherapy +14

Clinical and genetic profile of patients enrolled in the Transthyretin Amyloidosis Outcomes Survey (THAOS): 14-year update

Angela Dispenzieri, Teresa Coelho, Isabel Conceição et al. · Orphanet Journal of Rare Diseases · 2022 · 89 citations · Full text

Life Sciences, Genetics, Molecular Genetics +13

Characteristics of Patients with Late- vs. Early-Onset Val30Met Transthyretin Amyloidosis from the Transthyretin Amyloidosis Outcomes Survey (THAOS)

Márcia Waddington‐Cruz, Jonas Wixner, Leslie Amass et al. · Neurology and Therapy · 2021 · 47 citations · Full text

Life Sciences, Genetics, Neurology +9