Christine DeAntonis

Long-term efficacy and safety of mRNA therapy in two murine models of methylmalonic acidemia

An Ding, Andrea Frassetto, Eric Jacquinet et al. · EBioMedicine · 2019 · 84 citations · Full text

Life Sciences, Biochemistry, Pharmacology +16

Novel mRNA-Based Therapy Reduces Toxic Galactose Metabolites and Overcomes Galactose Sensitivity in a Mouse Model of Classic Galactosemia

Bijina Balakrishnan, An Ding, Vi Nguyen et al. · Molecular Therapy · 2019 · 60 citations · Full text

Life Sciences, Biochemistry, Genetics +16

Improved therapeutic efficacy in two mouse models of methylmalonic acidemia (MMA) using a second-generation mRNA therapy

Kimberly A. Coughlan, Marianne Eybye, Nicholas Henderson et al. · Molecular Genetics and Metabolism · 2024 · 18 citations

Life Sciences, Molecular Biology, Pharmacology +12

Messenger RNA rescues medium-chain acyl-CoA dehydrogenase deficiency in fibroblasts from patients and a murine model

Xuejun Zhao, Al‐Walid Mohsen, Stephanie J. Mihalik et al. · Human Molecular Genetics · 2023 · 13 citations · Full text

Life Sciences, Biochemistry, Molecular Biology +17