Oscar Della Pasqua

Double-blind, randomized, placebo-controlled study of trofinetide in pediatric Rett syndrome

Daniel G. Glaze, Jeffrey L. Neul, Walter E. Kaufmann et al. · Neurology · 2019 · 164 citations · Full text

What is the right dose for children?

Massimo Cella, Catherijne A. J. Knibbe, Meindert Danhof et al. · British Journal of Clinical Pharmacology · 2009 · 144 citations · Full text

A Phase 2 Study of AMO-02 (Tideglusib) in Congenital and Childhood-Onset Myotonic Dystrophy Type 1 (DM1)

Joseph P. Horrigan, Tiago Gomes, Mike Snape et al. · Pediatric Neurology · 2020 · 83 citations · Full text

Evaluation of the efficacy and safety of deferiprone compared with deferasirox in paediatric patients with transfusion-dependent haemoglobinopathies (DEEP-2): a multicentre, randomised, open-label, non-inferiority, phase 3 trial

Aurelio Maggio, Antonis Kattamis, Mariagrazia Felisi et al. · The Lancet Haematology · 2020 · 68 citations

Drug Safety, Transfusion-dependent Haemoglobinopathies, Pediatric Hematology +8

Dose optimization of piperacillin/tazobactam in critically ill children

Pieter De Cock, Sven C. van Dijkman, Annick De Jaeger et al. · Journal of Antimicrobial Chemotherapy · 2017 · 62 citations · Full text