Andrea Swenson

Safety and efficacy of eculizumab in anti-acetylcholine receptor antibody-positive refractory generalised myasthenia gravis (REGAIN): a phase 3, randomised, double-blind, placebo-controlled, multicentre study

James F. Howard, Kimiaki Utsugisawa, Michael Benatar et al. · The Lancet Neurology · 2017 · 800 citations

Medicine, Pharmacology, Pharmacotherapy +6

Trial of Sodium Phenylbutyrate–Taurursodiol for Amyotrophic Lateral Sclerosis

Sabrina Paganoni, Eric A. Macklin, Suzanne Hendrix et al. · New England Journal of Medicine · 2020 · 524 citations · Full text

Medicine, Neurology, Pharmacology +14

Safety and efficacy of avalglucosidase alfa versus alglucosidase alfa in patients with late-onset Pompe disease (COMET): a phase 3, randomised, multicentre trial

Jordi Díaz‐Manera, Priya S. Kishnani, Hani Kushlaf et al. · The Lancet Neurology · 2021 · 184 citations · Full text

Veterinary Medicine, Internal Medicine, Pharmacotherapy +3

Long‐term survival of participants in the <scp>CENTAUR</scp> trial of sodium phenylbutyrate‐taurursodiol in <scp>amyotrophic lateral sclerosis</scp>

Sabrina Paganoni, Suzanne Hendrix, Samuel P. Dickson et al. · Muscle & Nerve · 2020 · 180 citations · Full text

Medicine, Neurology, Pharmacology +15

A randomized controlled trial of methotrexate for patients with generalized myasthenia gravis

Mamatha Pasnoor, Jianghua He, Ted M. Burns et al. · Neurology · 2016 · 131 citations · Full text

Medicine, Pharmacology, Pharmacotherapy +14