Arnulfo Pie

Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B

Amit C. Nathwani, Edward G. D. Tuddenham, Savita Rangarajan et al. · New England Journal of Medicine · 2011 · 1.8K citations · Full text

Medicine, Hematology, Molecular Medicine +13

Sustained Clinical Benefit of AAV Gene Therapy in Severe Hemophilia B

Ulrike M. Reiss, Andrew M. Davidoff, Edward G. D. Tuddenham et al. · New England Journal of Medicine · 2025 · 49 citations · Full text

Medicine, Hematology, Molecular Medicine +13

GO-8: Stable Expression of Factor VIII over 5 Years Following Adeno-Associated Gene Transfer in Subjects with Hemophilia a Using a Novel Human Factor VIII Variant

Pratima Chowdary, Ulrike M. Reiss, Edward G. D. Tuddenham et al. · Blood · 2023 · 16 citations

Medicine, Hematology, Molecular Medicine +13

Stable Therapeutic Transgenic FIX Levels for More Than 10 Years in Subjects with Severe Hemophilia B Who Received scAAV2/8-LP1-Hfixco Adeno-Associated Virus Gene Therapy

Ulrike M. Reiss, Andrew M. Davidoff, Edward G. D. Tuddenham et al. · Blood · 2023 · 15 citations

Medicine, Molecular Biology, Molecular Medicine +13