Selina A. Azam

Restoration of vision after transplantation of photoreceptors

R. A. Pearson, Amanda C. Barber, Matteo Rizzi et al. · Nature · 2012 · 492 citations

Medicine, Ophthalmology, Surgery +10

Purification of recombinant adeno-associated virus type 8 vectors by ion exchange chromatography generates clinical grade vector stock

Andrew M. Davidoff, Catherine Y. Ng, Susan Sleep et al. · Journal of Virological Methods · 2004 · 121 citations

Life Sciences, Biotechnology, Molecular Biology +15

Gene therapy restores vision in rd1 mice after removal of a confounding mutation in Gpr179

Koji Nishiguchi, Lívia S. Carvalho, Matteo Rizzi et al. · Nature Communications · 2015 · 97 citations · Full text

Medicine, Genetics, Molecular Genetics +13

Long-Term Preservation of Cones and Improvement in Visual Function Following Gene Therapy in a Mouse Model of Leber Congenital Amaurosis Caused by Guanylate Cyclase-1 Deficiency

Marija Mihelec, R. A. Pearson, Scott Robbie et al. · Human Gene Therapy · 2011 · 72 citations · Full text

Medicine, Genetics, Ophthalmology +17

Prevention of Photoreceptor Cell Loss in a Cln6 Mouse Model of Batten Disease Requires CLN6 Gene Transfer to Bipolar Cells

Sophia-Martha kleine Holthaus, Joana Ribeiro, Laura Abelleira‐Hervas et al. · Molecular Therapy · 2018 · 45 citations · Full text

Medicine, Ophthalmology, Vision Science +17