Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

Alexis A. Thompson, Mark C. Walters, Janet L. Kwiatkowski, +44

New England Journal of Medicine

Treatment of Anaplastic Histology Wilms' Tumor: Results From the Fifth National Wilms' Tumor Study

Jeffrey S. Dome, Cecilia A. Cotton, Elizabeth J. Perlman, +15

Journal of Clinical Oncology

Association of busulfan exposure with survival and toxicity after haemopoietic cell transplantation in children and young adults: a multicentre, retrospective cohort analysis

Imke H. Bartelink, Arief Lalmohamed, Elisabeth M L van Reij, +29

The Lancet Haematology

Haemopoietic Cell TransplantationBusulfan ExposureTransplantationAllergyBone Marrow Failure +8

Autologous hematopoietic stem cell transplantation in patients with refractory Crohn’s disease

Yu Oyama, Robert M. Craig, Ann Traynor, +10

Gastroenterology

Cell TherapyTransplantationAutoimmune DiseaseMarrow TransplantationIntestinal Transplantation +6

Immune reconstitution and survival of 100 SCID patients post–hematopoietic cell transplant: a PIDTC natural history study

Jennifer Heimall, Brent R. Logan, Morton J. Cowan, +34

Blood

Treatment of Wilms tumor relapsing after initial treatment with vincristine, actinomycin D, and doxorubicin. A report from the National Wilms Tumor Study Group

Marcio H. Malogolowkin, Cecilia A. Cotton, Daniel M. Green, +21

Pediatric Blood & Cancer

Treatment With Nephrectomy Only for Small, Stage I/Favorable Histology Wilms’ Tumor: A Report From the National Wilms’ Tumor Study Group

Daniel M. Green, Norman E. Breslow, J. Bruce Beckwith, +19

Journal of Clinical Oncology

SCID genotype and 6-month posttransplant CD4 count predict survival and immune recovery

Élie Haddad, Brent R. Logan, Linda M. Griffith, +62

Blood

Neural Cell Differentiation In Vitro from Adult Human Bone Marrow Mesenchymal Stem Cells

Xiaoxiao Long, Marie Olszewski, Wei Huang, +1

Stem Cells and Development

Adult Stem CellCell DifferentiationBiomedical EngineeringNeural Cell DifferentiationRegenerative Medicine +15

Reduced intensity haemopoietic stem-cell transplantation for treatment of non-malignant diseases in children

David A. Jacobsohn, Reggie Duerst, William Tse, +1

The Lancet

Cell TherapyTransplantationMarrow TransplantationPediatric HematologyStem Cell Transplantation +6