Tohru Hirato

A Blood-Brain-Barrier-Penetrating Anti-human Transferrin Receptor Antibody Fusion Protein for Neuronopathic Mucopolysaccharidosis II

Hiroyuki Sonoda, Hideto Morimoto, Eiji Yoden et al. · Molecular Therapy · 2018 · 196 citations · Full text

Iduronate-2-Sulfatase with Anti-human Transferrin Receptor Antibody for Neuropathic Mucopolysaccharidosis II: A Phase 1/2 Trial

Torayuki Okuyama, Yoshikatsu Eto, Norio Sakai et al. · Molecular Therapy · 2018 · 150 citations · Full text

Phase 1/2, Translational Medicine, Autoimmune Disease +14

Mesenchymal Stem Cells Overexpressing Interleukin-10 Promote Neuroprotection in Experimental Acute Ischemic Stroke

Masataka Nakajima, Chikako Nito, Kota Sowa et al. · Molecular Therapy — Methods & Clinical Development · 2017 · 135 citations · Full text

Enzyme replacement therapy (ERT) procedure for mucopolysaccharidosis type II (MPS II) by intraventricular administration (IVA) in murine MPS II

Takashi Higuchi, Hiromi Shimizu, Takahiro Fukuda et al. · Molecular Genetics and Metabolism · 2012 · 46 citations

Ophthalmology, Enzyme Replacement Therapy, Mps Ii +2

Coformulation of a Novel Human α -Galactosidase A With the Pharmacological Chaperone AT1001 Leads to Improved Substrate Reduction in Fabry Mice

Su Xu, Yi Lun, Nastry Brignol et al. · Molecular Therapy · 2015 · 36 citations · Full text