Anne Malfroot

Ataluren for the treatment of nonsense-mutation cystic fibrosis: a randomised, double-blind, placebo-controlled phase 3 trial

Eitan Kerem, Michael W. Konstan, K. De Boeck et al. · The Lancet Respiratory Medicine · 2014 · 333 citations · Full text

Allergy, Placebo-controlled Phase 3, Clinical Trials +3

Efficacy and safety of lumacaftor and ivacaftor in patients aged 6–11 years with cystic fibrosis homozygous for F508del-CFTR : a randomised, placebo-controlled phase 3 trial

Félix Ratjen, Christopher Hug, Gautham Marigowda et al. · The Lancet Respiratory Medicine · 2017 · 291 citations

Pulmonary Fibrosis, Medicine, Placebo-controlled Phase 3

The ciliopathy-associated CPLANE proteins direct basal body recruitment of intraflagellar transport machinery

Michinori Toriyama, Chanjae Lee, S. Paige Taylor et al. · Nature Genetics · 2016 · 170 citations · Full text

Signal Transduction, Intraflagellar Transport Machinery, Intracellular Transport +13

Ferrous Iron Is a Significant Component of Bioavailable Iron in Cystic Fibrosis Airways

Ryan C. Hunter, Fadi Asfour, Jozef Dingemans et al. · mBio · 2013 · 167 citations · Full text

Gastro-oesophageal reflux and aspiration of gastric contents in adult patients with cystic fibrosis

Kathleen Blondeau, Lieven Dupont, Veerle Mertens et al. · Gut · 2008 · 152 citations