Laure Caccavelli

Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1

Salima Hacein‐Bey‐Abina, Alexandrine Garrigue, Gary P. Wang et al. · Journal of Clinical Investigation · 2008 · 1.8K citations · Full text

Viral Replication, Mixed-phenotype Acute Leukemia, Immunology +23

Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy

Nathalie Cartier, Salima Hacein‐Bey‐Abina, Cynthia C. Bartholomae et al. · Science · 2009 · 1.5K citations · Full text

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

Marina Cavazzana, Emmanuel Payen, Olivier Nègre et al. · Nature · 2010 · 1.3K citations

Hmga2 Activation, Transfusion Independence, Genetics +7

Gene Therapy in a Patient with Sickle Cell Disease

Jean‐Antoine Ribeil, Salima Hacein‐Bey‐Abina, Emmanuel Payen et al. · New England Journal of Medicine · 2017 · 658 citations · Full text

Immunohematology, Gene Therapies, Busulfan Conditioning +15

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

Alexis A. Thompson, Mark C. Walters, Janet L. Kwiatkowski et al. · New England Journal of Medicine · 2018 · 646 citations · Full text