Mariko Yamaoka

A Phase 2/3 Trial of Pabinafusp Alfa, IDS Fused with Anti-Human Transferrin Receptor Antibody, Targeting Neurodegeneration in MPS-II

Torayuki Okuyama, Yoshikatsu Eto, Norio Sakai et al. · Molecular Therapy · 2020 · 173 citations · Full text

Medicine, Neurology, Pharmacology +17

Bone marrow-derived mesenchymal stem cells (JR-031) for steroid-refractory grade III or IV acute graft-versus-host disease: a phase II/III study

Kazuo Muroi, Koichi Miyamura, Masaya Okada et al. · International Journal of Hematology · 2015 · 170 citations

Life Sciences, Cell Biology, Immunology +14

Iduronate-2-Sulfatase with Anti-human Transferrin Receptor Antibody for Neuropathic Mucopolysaccharidosis II: A Phase 1/2 Trial

Torayuki Okuyama, Yoshikatsu Eto, Norio Sakai et al. · Molecular Therapy · 2018 · 152 citations · Full text

Medicine, Neurology, Pharmacology +6

Iduronate-2-sulfatase fused with anti-hTfR antibody, pabinafusp alfa, for MPS-II: A phase 2 trial in Brazil

Roberto Giugliani, Ana Maria Martins, Sairei So et al. · Molecular Therapy · 2021 · 61 citations · Full text

Life Sciences, Neurology, Neuroscience +11

Enzyme Replacement Therapy with Pabinafusp Alfa for Neuronopathic Mucopolysaccharidosis II: An Integrated Analysis of Preclinical and Clinical Data

Roberto Giugliani, Ana Maria Martins, Torayuki Okuyama et al. · International Journal of Molecular Sciences · 2021 · 44 citations · Full text

Medicine, Neurology, Pharmacology +17