Jennifer Rothman

Hydroxycarbamide versus chronic transfusion for maintenance of transcranial doppler flow velocities in children with sickle cell anaemia—TCD With Transfusions Changing to Hydroxyurea (TWiTCH): a multicentre, open-label, phase 3, non-inferiority trial

Russell E. Ware, Barry R. Davis, William H. Schultz et al. · The Lancet · 2015 · 514 citations · Full text

Medicine, Hematology, Pediatrics +12

Clinical spectrum of pyruvate kinase deficiency: data from the Pyruvate Kinase Deficiency Natural History Study

Rachael F. Grace, Paola Bianchi, Eduard J. van Beers et al. · Blood · 2018 · 163 citations · Full text

Life Sciences, Biochemistry, Physiology +9

Randomized Placebo-Controlled Crossover Trial of Tadalafil in Raynaud’s Phenomenon Secondary to Systemic Sclerosis

Elena Schiopu, Vivien Hsu, Ann Impens et al. · The Journal of Rheumatology · 2009 · 105 citations · Full text

Medicine, Pharmacology, Pharmacotherapy +12

Mitapivat versus Placebo for Pyruvate Kinase Deficiency

Hanny Al‐Samkari, F. Galactéros, Andreas Glenthøj et al. · New England Journal of Medicine · 2022 · 94 citations · Full text

Medicine, Hematology, Pharmacology +13

Effects of hydroxyurea treatment for patients with hemoglobin <scp>SC</scp> disease

Lori Luchtman‐Jones, Sara Pressel, Lee Hilliard et al. · American Journal of Hematology · 2015 · 80 citations

Medicine, Hematology, Pharmacotherapy +12