Claudio Cherchi

Onasemnogene abeparvovec in spinal muscular atrophy: predictors of efficacy and safety in naïve patients with spinal muscular atrophy and following switch from other therapies

Marika Pane, Beatrice Berti, Anna Capasso et al. · EClinicalMedicine · 2023 · 46 citations · Full text

Pharmacy, Pediatrics, Pharmacotherapy +13

Hepatobiliary disease in XLMTM: a common comorbidity with potential impact on treatment strategies

Adele D’Amico, A Longo, Fabiana Fattori et al. · Orphanet Journal of Rare Diseases · 2021 · 33 citations · Full text

Medicine, Molecular Genetics, Molecular Medicine +13

Effects of the COVID‐19 pandemic and lockdown on symptom control in preschool children with recurrent wheezing

Nicola Ullmann, Annalisa Allegorico, Andrew Bush et al. · Pediatric Pulmonology · 2021 · 28 citations · Full text

Public Health, Child Health, Pediatrics +13

Results of Whole Brain Radiation Therapy in Patients with Brain Metastases from Colorectal Carcinoma

Maurizio Amichetti, Giancarlo Lay, Marina Dessì et al. · Tumori Journal · 2005 · 28 citations

Medicine, Oncology, Radiation Oncology +15

Neurocognitive profile of a cohort of SMA type 1 pediatric patients and emotional aspects, resilience and coping strategies of their caregivers

Michele Tosi, Francesca Cumbo, Michela Catteruccia et al. · European Journal of Paediatric Neurology · 2023 · 25 citations

Education, Behavioral Sciences, Pediatrics +17