Marina M. Scotti

Muscleblind-like 2-Mediated Alternative Splicing in the Developing Brain and Dysregulation in Myotonic Dystrophy

Konstantinos Charizanis, Kuang-Yung Lee, Ranjan Batra et al. · Neuron · 2012 · 348 citations · Full text

Medicine, Molecular Genetics, Neuroscience +15

Disrupted prenatal RNA processing and myogenesis in congenital myotonic dystrophy

James D. Thomas, Łukasz J. Sznajder, Olgert Bardhi et al. · Genes & Development · 2017 · 103 citations · Full text

Life Sciences, Genetics, Molecular Genetics +16

Scalable Recombinant Adeno-Associated Virus Production Using Recombinant Herpes Simplex Virus Type 1 Coinfection of Suspension-Adapted Mammalian Cells

Darby L. Thomas, Lijun Wang, Justine Niamke et al. · Human Gene Therapy · 2009 · 94 citations

Life Sciences, Biotechnology, Molecular Biology +15

An efficient rHSV-based complementation system for the production of multiple rAAV vector serotypes

Wen Kang, L Wang, Heather Harrell et al. · Gene Therapy · 2008 · 55 citations

Life Sciences, Biotechnology, Genetics +13

HNRNPA1-induced spliceopathy in a transgenic mouse model of myotonic dystrophy

Moyi Li, Yan Zhuang, Ranjan Batra et al. · Proceedings of the National Academy of Sciences · 2020 · 55 citations · Full text

Life Sciences, Genetics, Molecular Biology +16